April 14 – April 15, 2026
Arlington, VA
April 14 – April 15, 2026
Arlington, VA
When you join us for the NORD Rare Disease Scientific Symposium, you’ll engage with – and learn from – world-class rare disease researchers and experts. From academia and clinical settings to industry and regulatory bodies, our speakers will share cutting-edge research and inspire new collaboration.
Founder & Chief Executive Officer
Rarity PBC
Director
National Institutes of Health
Johns Hopkins University
Director, Office of Neuroscience
CDER, FDA
Director of Strategic Coalitions
FDA Rare Disease Innovation Hub
Assistant in Medicine, Division of Genetics and Genomics
Boston Children's Hospital
University of Michigan, Rogel Cancer Center
Assistant Professor of Neurology and Developmental Medicine
Kennedy Krieger Institute
CEO
EB Research Partnership
Professor of Biostatistics
University of Chicago
Professor of Biostatistics, Interim Associate Dean of Faculty Affairs
University of Michigan School of Public Health
Chief Scientific Officer
Foundation Fighting Blindness
Regulatory Scientist
FDA
VP of Clinical Development
uniQure
Statistician
FDA
Co-Founder
TANGO2 Research Foundation
Vice President, Medical Affairs
Lundbeck
Chief Medical Officer
Blood Cancer United
Medical Geneticist
Mayo Clinic
Director, US Medical Affairs
Takeda
Professor of Pediatrics
Stanford University
Assistant Professor of Genetics
Albert Einstein College of Medicine
Executive Director, Therapeutic Strategy Lead, Rare Disease & Cellular and Genetic Medicines
Worldwide Clinical Trials
Assistant Professor of Medical Ethics and Health Policy
University of Pennsylvania
Regulatory Affairs Leader
Former HHS
Health Science Policy Analyst
FDA
Director of Research Programs
Foundation for Prader-Willi Research
ASGCT
Vice President, Rare Disease, Center of Excellence
AESARA
Senior Director, Head of Quantitative Systems Pharmacology -US, R&D
Sanofi