Innovations in Drug Repurposing for Rare Diseases

Drug repurposing seeks to identify new disease applications for existing therapies. This session will provide an overview of how repurposing approaches are being explored in rare diseases and why they may offer a pragmatic path to treatment development when traditional discovery and development models are not feasible.

Moderator: Tracey Sikora, Vice President of Research and Clinical Programs, NORD 

Panelists:

• Heather Stone, MPH, Health Science Policy Analyst, FDA
• C. Lee Cohen, MD, MBA, Medical Officer, CDER, FDA
• Sarah Fuchs, MD, MSCI, Medical Officer, CDER, FDA
• Kasha Morris, MEd, Co-Founder, TANGO2 Research Foundation
• Savannah Latimer, Clinical Research Assistant, Division of Emergency Medicine, Children’s National Hospital, a NORD Rare Disease Center of Excellence
• Maurice Leary, Children’s National Hospital, a NORD Rare Disease Center of Excellence
• Natasha Shur, MD, Medical Geneticist, Professor of Pediatrics, Children’s National Hospital, a NORD Rare Disease Center of Excellence

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