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What to Expect

Discover the power of collaboration

Advancing Rare Disease Research Together

Join top researchers, clinicians, regulators, and industry leaders to explore groundbreaking advancements in rare disease science. Engage in expert-led discussions, discover innovative research approaches, and collaborate with leaders shaping the future of rare disease research and care.

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Attendees

  • Medical Professionals and Researchers

    • Learn more about emerging advancements in rare disease research, clinical trials, and translational science.
    • Network with leading experts across multiple specialties to foster new collaborations.

  • Pharma/Biotech

    • Connect with leading researchers and clinicians to explore potential partnerships.
    • Learn about innovative trial designs and real-world data applications in rare disease research.

  • Regulators

    • Engage in discussions on clinical trial methodologies and applications of real-world data, focusing on the unique challenges of rare disease research.
    • Connect with the researchers, clinicians, and industry leaders who are leading discussions on policy and regulation.

  • Patient Organizations and Advocates

    • Learn about the latest scientific breakthroughs and how they impact the rare disease community.
    • Connect with researchers and industry leaders to advocate for patient-driven research.
    • Explore opportunities to collaborate on advancing clinical research and therapeutic development.